fabry's disease Clinical Research Trials

Found 3 clinical trials

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For Seniors
For adults
Recruiting in 10s
Interventional Study
For Males
Gastroenterology
Recruiting

A Long Term Follow-Up Study of Fabry Disease Subjects Treated With FLT190

Fabry disease is a rare, X-linked inborn error of glycosphingolipid metabolism caused by an abnormal gene encoding the -galactosidase A (GLA) enzyme.

deficiency

breakdown

gene therapy

glycosphingolipids

fabry's disease

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19 Feb, 2024

Multi-country trial
Phase 3
Recruiting in 1000s
Observational Study
all
Recruiting

Fabry Disease Registry & Pregnancy Sub-registry

The Fabry Registry is an ongoing, international multi-center, strictly observational program that tracks the routine clinical outcomes for patients with Fabry disease, irrespective of treatment status.

deficiency

replacement therapy

fabrazyme

alpha-galactosidase

agalsidase beta

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05 Aug, 2024
126 locations

For pediatric ages
For Seniors
Recruiting in 10s
Observational Study
For Females
Gastroenterology
Recruiting

A Global Prospective Observational Study of Women With Fabry Disease and Their Infants During Pregnancy and Breastfeeding

This is a global prospective observational study of women with Fabry disease and their infants during pregnancy and/or breastfeeding. The study will evaluate outcomes of pregnancy and/or breastfeeding in women and infants exposed to migalastat.

migalastat

fabry's disease

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19 Feb, 2024

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Found 3 clinical trials

A Long Term Follow-Up Study of Fabry Disease Subjects Treated With FLT190

Fabry Disease Registry & Pregnancy Sub-registry

A Global Prospective Observational Study of Women With Fabry Disease and Their Infants During Pregnancy and Breastfeeding