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Found 2 clinical trials
Featured trial
Fabry Disease Registry & Pregnancy Sub-registry (acronym)

The primary objectives of the Registry are:To enhance the understanding of the variability, progression, and natural history of Fabry disease, including heterozygous females with the disease;To assist the Fabry medical community with the development of recommendations for monitoring patients and reports on patient outcomes to help optimize patient care;To characterize …

  • 0 views
  • 21 May, 2025
Fabry Disease Registry & Pregnancy Sub-registry

The primary objectives of the Registry are: To enhance the understanding of the variability, progression, and natural history of Fabry disease, including heterozygous females with the disease; To assist the Fabry medical community with the development of recommendations for monitoring patients and reports on patient outcomes to help optimize patient …

fabry's disease
fabrazyme
deficiency
replacement therapy
alpha-galactosidase
  • 0 views
  • 05 Aug, 2024
  • 126 locations